Baby with SMA holding the hand of a healthcare profressional with a DNA strand in the background

A doctor and a patient connecting over the one-time-only infusion of ZOLGENSMA

The one-time-only dose to stop SMA progression

ZOLGENSMA® (onasemnogene abeparvovec-xioi)  is a gene therapy for pediatric patients less than 2 years of age with spinal muscular atrophy (SMA)1

SEE EFFICACY DATA

Complete Phase 3 SPR1NT data is available

The SPR1NT clinical trial is complete for presymptomatic patients with 2 and 3 copies of SMN2. View data for patients treated with ZOLGENSMA.

SEE PRESYMPTOMATIC DATA

ZOLGENSMA patient combined prescription and patient consent form

Getting started with ZOLGENSMA

Complete the ZOLGENSMA Prescription and Patient Consent Forms for eligible patients to help with insurance and prescription-related processes.

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Spinal muscular atrophy (SMA) ZOLGENSMA patient Lucy laying on the floor demonstrating head control

Explore Lucy’s ZOLGENSMA journey

Lucy was identified by newborn screening in her state and treated at ~5 weeks old. Learn about her SMA treatment journey now that she’s ~1 year old.

SEE PATIENT PROFILE

LOCATE A REP

Enter your ZIP code to locate your nearest Novartis Gene Therapies representative to guide you and your patients throughout the ZOLGENSMA treatment process.

You must enter a valid ZIP code. E.g. 90210

RESOURCES

Visit the Resources page to learn more about ZOLGENSMA. Here, you’ll be able to access additional data through scientific reprints, access pre- and posttreatment guides, and important forms.

RESOURCES
OneGene Program Logo | ZOLGENSMA® (onasemnogene abeparvovec-xioi)

Patient support

The OneGene Program®, offered by Novartis Gene Therapies, is a comprehensive, individualized support program for families with pediatric patients less than 2 years of age with spinal muscular atrophy (SMA) and their healthcare providers throughout the ZOLGENSMA treatment journey.

OneGene Program support includes:
  • Answers to questions about ZOLGENSMA
  • A dedicated, personalized support team focused on the needs of each family
  • Verification of insurance benefits
  • Coordination of financial assistance programs for eligible patients

Families can access the full range of OneGene Program support resources when the ZOLGENSMA Prescription Form and accompanying Patient Consent Form have been provided to the OneGene Program.

For questions call 1-855-441-GENE (4363),
Monday-Friday (8 AM to 8 PM ET)

For questions call 1-855-441-GENE (4363) – Monday-Friday (8 AM to 8 PM ET)

Discover more about ZOLGENSMA

About ZOLGENSMA

Explore efficacy, safety, dosing, and how ZOLGENSMA works

About ZOLGENSMA

Understand SMA

Learn about the signs and symptoms of SMA

Understand SMA

Steps to treatment

What to know before, during, and after infusion day

Steps to treatment

Resources

Learn about resources available to your patients

Resources

Reference: 1. ZOLGENSMA [prescribing information]. Bannockburn, IL: Novartis Gene Therapies, Inc; 2021.