The one-time-only dose to stop SMA progression
ZOLGENSMA® is a gene therapy for pediatric patients less than 2 years of age with spinal muscular atrophy (SMA)1

Getting started with ZOLGENSMA
Complete the ZOLGENSMA Prescription and Patient Consent Forms for eligible patients to help with insurance and prescription-related processes.
OneGene Program
Patient support
The OneGene Program™, offered by AveXis, is a comprehensive, individualized support program for families with pediatric patients less than 2 years of age with spinal muscular atrophy (SMA) and their healthcare providers throughout the ZOLGENSMA® (onasemnogene abeparvovec-xioi) treatment journey.
OneGene Program support includes:
- Answers to questions about ZOLGENSMA
- A dedicated, personalized support team focused on the needs of each family
- Verification of insurance benefits
- Coordination of financial assistance programs for eligible patients
Families can access the full range of OneGene Program support resources when the ZOLGENSMA Prescription Form and accompanying Patient Consent Form have been provided to the OneGene Program.
For questions call 1-855-441-GENE (4363),
Monday-Friday (8 AM to 8 PM ET)