Patient profiles

START patient stories

Stories from the Phase 1 trial

Adalyne 

Treated with ZOLGENSMA at ~2.5 months old, pictured here at ~4 years old 

Adalyne participated in the START clinical study; after completing the study, Adalyne started another disease-modifying treatment for SMA beginning at ~2.5 years old. To see Adalyne’s story, watch the video or download the PDF.

Adalyne’s Treatment Journey Timeline

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Real spinal muscular atrophy (SMA) Type 1 patient Adalyne smiling and sitting up

*As of December 2019. 

Matteo  

Treated with ZOLGENSMA at ~1 month old, pictured here at ~4 years old 

To see Matteo’s story, watch the video or download the PDF.

Matteo’s Treatment Journey Timeline

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Real spinal muscular atrophy (SMA) Type 1 ZOLGENSMA patient Matteo smiling

*As of December 2019. 

Louis 

Treated with ZOLGENSMA at ~2.5 months old, pictured here at ~3 years old

To see Louis’ story, watch the video or download the PDF.

Louis’ Treatment Journey Timeline

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Real spinal muscular atrophy (SMA) Type 1 ZOLGENSMA patient Louis with his mother playing on the monkey bars on the playground

*As of December 2019. 

Steps to Treatment

What to know before, during and after infusion day

Steps to Treatment

STR1VE Trial

A Phase 3 clinical trial

STR1VE Trial