Real patient stories
See the results with one-time-only gene therapy.
Maisie
Treated with ZOLGENSMA at ~20 months old, pictured here at ~2 years old
Maisie also received another disease-modifying treatment for SMA from ~6 months to ~20 months. To see Maisie’s story, watch the video or download the PDF.
Maisie’s Treatment Journey Timeline
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*As of December 2019.
Louis
Treated with ZOLGENSMA at ~2.5 months old, pictured here at ~4.5 years old*
To see Louis’ story, watch the video or download the PDF.
*As of Dec 2019.
Louis’ Treatment Journey Timeline
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*As of December 2019.
Adalyne
Treated with ZOLGENSMA at ~2.5 months old, pictured here at ~4.5 years old*
Adalyne participated in the START clinical study; after completing the study, Adalyne started another disease-modifying treatment for SMA beginning at ~2.5 years old. To see Adalyne’s story, watch the video or download the PDF.
*As of Dec 2019.
Adalyne’s Treatment Journey Timeline
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*As of December 2019.
